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CLINICAL_TRIALS trial_result · 2026-03-18

Clinical Trial Update: Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett Syndrome [Phase 3]

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Summary

Phase 3 clinical trial update for TSHA-102 gene therapy in young girls with Rett syndrome, focusing on safety and preliminary efficacy, with the study currently…

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Diseases / indications

Drugs mentioned

  • TSHA-102

Snippet

Sponsor: Taysha Gene Therapies, Inc. | Conditions: Rett Syndrome | Phase 3 | Status: NOT_YET_RECRUITING