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CLINICAL_TRIALS research · 2026-03-13

Clinical Trial Update: A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome [Phase 3]

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Summary

A Phase 3 clinical trial to evaluate NGN-401, a gene therapy, for Rett syndrome in females is currently recruiting.

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Diseases / indications

Drugs mentioned

  • NGN-401

Snippet

Sponsor: Neurogene Inc. | Conditions: Rett Syndrome | Phase 3 | Status: RECRUITING