Quadriceps Sparing Myopathy

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CLINICAL_TRIALS trial_result · 2019-02-19
Clinical Trial Update: Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With Glucosamine (UDP-N-acetyl)-2-epimerase Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM) [Phase 3]
Phase 3 trial evaluating Ace-ER in GNEM/HIBM was terminated; results were posted in 2019.