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CLINICAL_TRIALS ClinicalTrials.gov record update

Phase 3B Open-Label Extension Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)

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Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT02736188
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-28T10:39:15.159009+00:00
Published At
2019-02-19T00:00:00+00:00
Record Updated At
2023-03-24
Results Posted At
2019-02-19
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Hereditary Inclusion Body Myopathy", "Distal Myopathy With Rimmed Vacuoles", "Distal Myopathy, Nonaka Type", "GNE Myopathy", "Quadriceps Sparing Myopathy"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2023-03-24"
protocolSection.identificationModule.nctId
"NCT02736188"
protocolSection.identificationModule.officialTitle
"Phase 3B Open-Label Extension Study to Evaluate the Safety and Efficacy of Aceneuramic Acid Extended-Release (Ace-ER) Tablets in Patients With GNE Myopathy (GNEM) or Hereditary Inclusion Body Myopathy (HIBM)"
protocolSection.statusModule.overallStatus
"TERMINATED"
protocolSection.designModule.phases
["PHASE3"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
"2019-02-19"

Study condition terms

  • Hereditary Inclusion Body Myopathy (protocolSection.conditionsModule.conditions)
  • Distal Myopathy With Rimmed Vacuoles (protocolSection.conditionsModule.conditions)
  • Distal Myopathy, Nonaka Type (protocolSection.conditionsModule.conditions)
  • GNE Myopathy (protocolSection.conditionsModule.conditions)
  • Quadriceps Sparing Myopathy (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.