Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS ClinicalTrials.gov record update

A Phase 2 Open-label Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER) Tablets in GNE Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy (HIBM)) Patients With Severe Ambulatory Impairment

This page presents selected fields from the linked source record. It does not add a medical interpretation.

Open original source record ↗

Record identity and dates

Source
ClinicalTrials.gov
Source record ID
NCT02731690
Title field or adapter rule
protocolSection.identificationModule.officialTitle
Ingested At
2026-04-28T10:37:00.278145+00:00
Published At
2019-02-19T00:00:00+00:00
Record Updated At
2019-02-19
Results Posted At
2019-02-19
Timestamp Basis
source retrieval time was not retained by the feed adapter
Date limitation
source retrieval time was not retained by the feed adapter

Fields recorded by this source

protocolSection.conditionsModule.conditions
["Hereditary Inclusion Body Myopathy", "Distal Myopathy With Rimmed Vacuoles", "Distal Myopathy, Nonaka Type", "GNE Myopathy", "Quadriceps Sparing Myopathy", "Inclusion Body Myopathy 2"]
protocolSection.statusModule.lastUpdatePostDateStruct.date
"2019-02-19"
protocolSection.identificationModule.nctId
"NCT02731690"
protocolSection.identificationModule.officialTitle
"A Phase 2 Open-label Study to Evaluate the Safety of Aceneuramic Acid Extended Release (Ace-ER) Tablets in GNE Myopathy (GNEM) (Also Known as Hereditary Inclusion Body Myopathy (HIBM)) Patients With Severe Ambulatory Impairment"
protocolSection.statusModule.overallStatus
"TERMINATED"
protocolSection.designModule.phases
["PHASE2"]
protocolSection.statusModule.resultsFirstPostDateStruct.date
"2019-02-19"

Study condition terms

  • Hereditary Inclusion Body Myopathy (protocolSection.conditionsModule.conditions)
  • Distal Myopathy With Rimmed Vacuoles (protocolSection.conditionsModule.conditions)
  • Distal Myopathy, Nonaka Type (protocolSection.conditionsModule.conditions)
  • GNE Myopathy (protocolSection.conditionsModule.conditions)
  • Quadriceps Sparing Myopathy (protocolSection.conditionsModule.conditions)
  • Inclusion Body Myopathy 2 (protocolSection.conditionsModule.conditions)

Intervention details are not present in the imported fields for this record. No drug-condition relationship is inferred from co-listing.

This index keeps the source fields it imported; it may not contain the complete original record. Verify wording and context in the linked source.