Ciliary Dyskinesia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Genetic Disorders of Mucociliary Clearance in Nontuberculous Mycobacterial Lung Disease
This completed NHLBI study examined genetic disorders that affect mucociliary clearance in nontuberculous mycobacterial lung disease, includ…
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: Developing Resource Interventions for Healthcare Professionals and Patients to Improve Knowledge About Fertility in Primary Ciliary Dyskinesia [NA]
Not-yet-recruiting clinical study from the University of Southampton developing resources to improve knowledge about fertility for people wi…
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CLINICAL_TRIALS research · 2026-02-20Clinical Trial Update: A Cohort for Inflammatory Respiratory Diseases: From Phenotyping to Personalised Medicine
A clinical trial update describes a cohort study aimed at phenotyping inflammatory respiratory diseases to enable personalised medicine, cur…
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CLINICAL_TRIALS trial_result · 2026-02-18Clinical Trial Update: Clean Air for Rare MUcociliary Clearance dIsorders [NA]
This clinical trial update indicates that a study addressing rare mucociliary clearance disorders, including Primary Ciliary Dyskinesia and …
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: DCP (RaDiCo Cohort) (RaDiCo-DCP)
A recruitment update for the RaDiCo-DCP RaDiCo cohort study sponsored by INSERM (Institut National de la Santé et de la Recherche Médicale) …
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CLINICAL_TRIALS trial_result · 2026-02-03Clinical Trial Update: Exercise Capacity, Muscle Oxygenation, Respiratory Muscle Strength, and Physical Activity Level in Pediatric CF and PCD
A completed clinical trial from Gazi University evaluating exercise capacity, muscle oxygenation, respiratory muscle strength, and physical …
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CLINICAL_TRIALS research · 2026-01-30Clinical Trial Update: Digital Physiotherapy for Pediatric Chronic Suppurative Lung Diseases [NA]
A clinical trial update describing a digital physiotherapy program for children with chronic suppurative lung diseases, including protracted…
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CLINICAL_TRIALS research · 2026-01-22Clinical Trial Update: A Qualitative Study Investigating the Lived Experiences and Impact of Reproductive Issues in Adults With Primary Ciliary Dyskinesia
This clinical trial update describes a qualitative study examining the lived experiences and impact of reproductive issues in adults with pr…
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CLINICAL_TRIALS research · 2025-12-19Clinical Trial Update: High Resolution Micro OCT Imaging
A clinical trial update indicates the High Resolution Micro OCT Imaging study led by the University of Alabama at Birmingham is currently ac…
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CLINICAL_TRIALS research · 2025-12-17Clinical Trial Update: Examining Bronchial Hyperresponsiveness in Primary Ciliary Dyskinesia [NA]
A clinical trial investigating bronchial hyperresponsiveness in individuals with Primary Ciliary Dyskinesia is currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-12-10Clinical Trial Update: Longitudinal Characterization of Respiratory Tract Exacerbations and Treatment Responses in Primary Ciliary Dyskinesia
This is a completed longitudinal clinical trial characterizing respiratory tract exacerbations and treatment responses in primary ciliary dy…
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CLINICAL_TRIALS research · 2025-12-02Clinical Trial Update: The Ear-Nose-Throat (ENT) Prospective International Cohort of PCD Patients (EPIC-PCD)
The EPIC-PCD study is an international prospective cohort investigating primary ciliary dyskinesia, including Kartagener syndrome. The study…
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CLINICAL_TRIALS research · 2025-12-02Clinical Trial Update: Living With Primary Ciliary Dyskinesia (Living With PCD)
Clinical trial update for a study on living with Primary Ciliary Dyskinesia, sponsored by the University of Bern, currently recruiting.
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CLINICAL_TRIALS research · 2025-11-25Clinical Trial Update: Swiss Primary Ciliary Dyskinesia Registry
This clinical trial update announces the Swiss Primary Ciliary Dyskinesia Registry, sponsored by the University of Bern, and indicates recru…
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CLINICAL_TRIALS trial_result · 2025-11-25Clinical Trial Update: Glycine and Magnesium+Thiamine for the Treatment of Primary Ciliary Dyskinesia [NA]
A clinical trial is recruiting to evaluate glycine and a magnesium plus thiamine combination for treating primary ciliary dyskinesia. The st…
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CLINICAL_TRIALS research · 2025-11-25Clinical Trial Update: International Primary Ciliary Dyskinesia Cohort
An international cohort study on primary ciliary dyskinesia and Kartagener syndrome is currently active but not recruiting.
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CLINICAL_TRIALS research · 2025-10-24Clinical Trial Update: Acoustic Waveform Respiratory Evaluation [NA]
This clinical trial evaluates acoustic waveform respiratory assessment across several respiratory diseases and is currently recruiting.
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CLINICAL_TRIALS research · 2025-10-20Clinical Trial Update: Study of Inhaled RCT1100 in Adults With PCD Caused by Pathogenic Mutations in the DNAI1 Gene to Measure Mucociliary Clearance [Phase 1]
A Phase 1 clinical trial evaluating inhaled RCT1100 in adults with Primary Ciliary Dyskinesia due to DNAI1 mutations, sponsored by ReCode Th…
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CLINICAL_TRIALS trial_result · 2025-10-08Clinical Trial Update: A Study to Assess the Safety, Tolerability, Ciliary Rescue, and Pharmacodynamics of RCT1100 in Adults With PCD [Phase 1]
This clinical trial update notes completion of a Phase 1 study evaluating the safety, tolerability, ciliary rescue, and pharmacodynamics of …
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CLINICAL_TRIALS trial_result · 2025-09-22Clinical Trial Update: Utility of PCD Diagnostics to Improve Clinical Care
This clinical trial update describes the ongoing study evaluating the utility of PCD diagnostics to improve clinical care for patients with …
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CLINICAL_TRIALS trial_result · 2025-09-08Clinical Trial Update: Upper Extremity Exercise Capacity, Muscle Oxygenation, and Balance in Pediatric CF and PCD
A pediatric trial evaluating upper-extremity exercise capacity, muscle oxygenation, and balance in cystic fibrosis and primary ciliary dyski…
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CLINICAL_TRIALS trial_result · 2025-09-05Clinical Trial Update: Functional Studies of Novel Genes Mutated in Primary Ciliary Dyskinesia II: Genotype to Phenotype [EARLY_Phase 1]
An early-phase functional genomics study investigates novel genes mutated in primary ciliary dyskinesia and explores genotype-to-phenotype r…
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CLINICAL_TRIALS trial_result · 2025-08-21Clinical Trial Update: Characterizing the Upper Airway Manifestations in Primary Ciliary Dyskinesia and Primary Immunodeficiencies
Completed clinical trial examining upper airway manifestations in primary ciliary dyskinesia and primary immunodeficiencies.
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CLINICAL_TRIALS trial_result · 2025-08-21Clinical Trial Update: Defining the Genetic Etiology of Suppurative Lung Disease in Children and Adults
This clinical trial update reports the completion of a study investigating the genetic basis of suppurative lung disease in children and adu…
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CLINICAL_TRIALS research · 2025-08-12Clinical Trial Update: CZI Rare As One: Co-designing an App and Wearable Based Compass for Rare Diseases
A completed clinical trial update about co-designing an app and wearable compass for rare diseases, covering chronic pancreatitis, sarcoidos…