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CLINICAL_TRIALS trial_result · 2025-09-05

Clinical Trial Update: Functional Studies of Novel Genes Mutated in Primary Ciliary Dyskinesia II: Genotype to Phenotype [EARLY_Phase 1]

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Summary

An early-phase functional genomics study investigates novel genes mutated in primary ciliary dyskinesia and explores genotype-to-phenotype relationships; result…

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Diseases / indications

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Sponsor: University of North Carolina, Chapel Hill | Conditions: Primary Ciliary Dyskinesia | EARLY_Phase 1 | Status: COMPLETED | Results posted: 2025-09-05