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CLINICAL_TRIALS research · 2025-10-20

Clinical Trial Update: Study of Inhaled RCT1100 in Adults With PCD Caused by Pathogenic Mutations in the DNAI1 Gene to Measure Mucociliary Clearance [Phase 1]

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Summary

A Phase 1 clinical trial evaluating inhaled RCT1100 in adults with Primary Ciliary Dyskinesia due to DNAI1 mutations, sponsored by ReCode Therapeutics, currentl…

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Diseases / indications

Drugs mentioned

  • RCT1100

Snippet

Sponsor: ReCode Therapeutics | Conditions: Primary Ciliary Dyskinesia (PCD) | Phase 1 | Status: ACTIVE_NOT_RECRUITING