Otoferlin-related Hearing Loss

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CLINICAL_TRIALS withdrawal · 2025-04-10
Clinical Trial Update: a Study in Subjects With Otoferlin Mutation-related Hearing Loss Using RNA Base-eDiting Therapy(SOUND) [EARLY_Phase 1]
The EARLY_PHASE1 trial of RNA Base-eDiting Therapy (SOUND) for otoferlin-related congenital hearing loss has been withdrawn.