Otoferlin-related Hearing Loss

Top drugs studied for this disease

All Approvals Safety alerts Label changes Trial results Research Guidance Withdrawals

CLINICAL_TRIALS trial_result · 2026-04-06
Clinical Trial Update: Long Term Follow-up Study of AAVAnc80-hOTOF Gene Therapy
A long-term follow-up study of the AAVAnc80-hOTOF gene therapy for otoferlin-related hearing loss is currently enrolling by invitation.