Otoferlin-related Hearing Loss
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CLINICAL_TRIALS trial_result · 2026-04-06Clinical Trial Update: Long Term Follow-up Study of AAVAnc80-hOTOF Gene Therapy
A long-term follow-up study of the AAVAnc80-hOTOF gene therapy for otoferlin-related hearing loss is currently enrolling by invitation.
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CLINICAL_TRIALS withdrawal · 2025-04-10Clinical Trial Update: a Study in Subjects With Otoferlin Mutation-related Hearing Loss Using RNA Base-eDiting Therapy(SOUND) [EARLY_Phase 1]
The EARLY_PHASE1 trial of RNA Base-eDiting Therapy (SOUND) for otoferlin-related congenital hearing loss has been withdrawn.