Neuronal Ceroid Lipofuscinosis
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies
An Italian Neuronal Ceroid Lipofuscinosis registry (NCL Registry) to integrate data and inform future therapeutic strategies for NCL; the st…
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CLINICAL_TRIALS research · 2025-10-24Clinical Trial Update: Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease
This update indicates an ongoing study evaluating developmental outcomes in children diagnosed with CLN2 disease (Batten disease), currently…
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CLINICAL_TRIALS research · 2025-10-02Clinical Trial Update: Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
This clinical trial update provides information on the long-term follow-up of CLN6-related Batten disease subjects after gene transfer; the …
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CLINICAL_TRIALS research · 2025-09-12Clinical Trial Update: Clinical and Neuropsychological Investigations in Batten Disease
This clinical trial at the University of Rochester investigates the clinical and neuropsychological aspects of Batten disease (neuronal cero…
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CLINICAL_TRIALS research · 2025-07-30Clinical Trial Update: Natural History of Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae
This clinical trial update describes a natural history study of Batten disease caused by CLN6 mutations (neuronal ceroid lipofuscinosis) and…
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CLINICAL_TRIALS trial_result · 2016-07-26Clinical Trial Update: Neuronal Ceroid Lipofuscinosis and Associated Sleep Abnormalities
A completed clinical trial sponsored by Nationwide Children's Hospital studied sleep abnormalities in people with Neuronal Ceroid Lipofuscin…
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CLINICAL_TRIALS withdrawal · 2015-01-15Clinical Trial Update: Safety and Efficacy Study of HuCNS-SC in Subjects With Neuronal Ceroid Lipofuscinosis [Phase 1]
Phase 1 safety and efficacy study of HuCNS-SC for Neuronal Ceroid Lipofuscinosis has been withdrawn.