Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS research · 2026-03-27

Clinical Trial Update: Italian NCL Registry: a Registry for NCL as an Integration Tool for Future Therapeutic Strategies

View source ↗

Summary

An Italian Neuronal Ceroid Lipofuscinosis registry (NCL Registry) to integrate data and inform future therapeutic strategies for NCL; the study is currently rec…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Snippet

Sponsor: IRCCS Fondazione Stella Maris | Conditions: Neuronal Ceroid Lipofuscinosis | Status: RECRUITING