Myotonic Dystrophy Type
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-11-24Clinical Trial Update: Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy
A Massachusetts General Hospital clinical trial is investigating cerebrospinal fluid biomarkers in myotonic dystrophy type 1. The study is c…
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CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: Study of ARO-DM1 in Subjects With Type 1 Myotonic Dystrophy [Phase 1, Phase 2]
Ongoing Phase 1/2 clinical trial evaluating ARO-DM1 in subjects with Myotonic Dystrophy Type 1, currently recruiting.
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CLINICAL_TRIALS research · 2025-10-15Clinical Trial Update: Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
A registry study update listing RECRUITING status for Myotonic Dystrophy type 1, Myotonic Dystrophy type 2, and Facioscapulohumeral muscular…
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CLINICAL_TRIALS trial_result · 2025-10-08Clinical Trial Update: Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients [Phase 2]
This clinical trials update reports the extension of the AOC 1001-CS1 (MARINA) study in adults with myotonic dystrophy type 1 (DM1). The Pha…
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CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: A Multicenter Phenotype-Genotype Analysis of DM1 Patients in China
A multicenter study from Huashan Hospital in China is conducting a phenotype-genotype analysis of patients with myotonic dystrophy type 1. T…
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CLINICAL_TRIALS trial_result · 2025-09-12Clinical Trial Update: Venous Thromboembolism in Myotonic Dystrophy Type 1 [NA]
The clinical trial NCT03424460 evaluating venous thromboembolism risk in patients with Myotonic Dystrophy Type 1 has completed. The sponsor …
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: Study of Tideglusib in Adolescent and Adult Patients With Myotonic Dystrophy [Phase 2]
A Phase 2 study of Tideglusib in adolescent and adult patients with myotonic dystrophy type 1 has completed and results have been posted.
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CLINICAL_TRIALS research · 2025-08-22Clinical Trial Update: Gait Analysis Parameter and Upper Limb Evaluation in Adult Patients With Neurological or Metabolic Pathology [NA]
This clinical trial update describes the assessment of gait analysis parameters and upper-limb evaluation in adults with various neurologica…
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CLINICAL_TRIALS trial_result · 2025-08-19Clinical Trial Update: Profile of Dysphagia in Myotonic Dystrophy Type 1 (DM1)
This clinical trial update describes the profile of swallowing difficulties (dysphagia) in individuals with Myotonic Dystrophy Type 1 and no…
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CLINICAL_TRIALS research · 2025-07-30Clinical Trial Update: Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
This clinical trial extension outlines plans to assess endpoints and trial readiness for a pediatric myotonic dystrophy study. It targets co…
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CLINICAL_TRIALS research · 2025-07-18Clinical Trial Update: The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Following a Training Period. [NA]
This clinical trial update outlines a study evaluating whether assistive gait devices, following a training period, can reduce fall risk in …
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CLINICAL_TRIALS research · 2025-06-11Clinical Trial Update: DMCRN-02-001: Assessing Pediatric Endpoints in DM1
A clinical trial (DMCRN-02-001) assessing pediatric endpoints in congenital myotonic dystrophy (DM1) is currently recruiting.
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CLINICAL_TRIALS research · 2025-06-06Clinical Trial Update: Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
This clinical trial update describes END-DM1, a Virginia Commonwealth University study to establish biomarkers and clinical endpoints for my…
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CLINICAL_TRIALS research · 2025-05-28Clinical Trial Update: Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy [Phase 2, Phase 3]
This clinical trial update notes a Phase 2/3 study evaluating tideglusib for congenital or childhood-onset myotonic dystrophy that is curren…
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CLINICAL_TRIALS research · 2025-05-23Clinical Trial Update: Myotonic Dystrophy - Vascular and Cognition
A clinical trial update indicates a study on myotonic dystrophy type 1 with vascular and cognitive focus is active but not currently recruit…
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CLINICAL_TRIALS research · 2025-05-20Clinical Trial Update: Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study [NA]
A clinical trial at Centre Hospitalier Universitaire de Liege assesses muscular pathology in patients and controls under the ActiLiège Next …
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CLINICAL_TRIALS research · 2025-05-18Clinical Trial Update: A Registered Observational Cohort Study of Myotonic Dystrophy Type 1
An observational registered cohort study of Myotonic Dystrophy Type 1 is currently enrolling by invitation.
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CLINICAL_TRIALS trial_result · 2025-04-27Clinical Trial Update: Symptoms and Outcome Measures for Upper- Limb Function in Myotonic Dystrophy Type 1
A completed clinical study evaluating symptoms and outcome measures for upper-limb function in individuals with myotonic dystrophy type 1.
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CLINICAL_TRIALS research · 2025-04-27Clinical Trial Update: Personalized Training for People With Rare Neuromuscular Disorders [NA]
A clinical trial update announcing recruitment for personalized training programs for people with rare neuromuscular disorders. The study ta…
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CLINICAL_TRIALS trial_result · 2025-04-25Clinical Trial Update: Safety and Efficacy of Pitolisant on Excessive Daytime Sleepiness and Other Non-Muscular Symptoms in Patients With Myotonic Dystrophy Type 1 [Phase 2]
A Phase 2 trial evaluated the safety and efficacy of pitolisant for excessive daytime sleepiness and other non-muscular symptoms in adults w…
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CLINICAL_TRIALS research · 2025-03-28Clinical Trial Update: A Remote Physical Activity Program in the Population Suffering from Type 1 Myotonic Dystrophy [NA]
A clinical trial update describing a remote physical activity program for individuals with myotonic dystrophy type 1 (DM1); the study status…
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CLINICAL_TRIALS research · 2025-02-24Clinical Trial Update: Pelvic Floor Muscle Training for Women with Myotonic Dystrophy [NA]
A clinical trial to assess pelvic floor muscle training in women with myotonic dystrophy type 1 and urinary incontinence is currently recrui…
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CLINICAL_TRIALS research · 2024-11-21Clinical Trial Update: Myotonic Dystrophy Family Registry
A clinical trial registry entry for the Myotonic Dystrophy Family Registry, currently recruiting to collect data on myotonic dystrophy types…
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CLINICAL_TRIALS research · 2024-09-19Clinical Trial Update: Wheelchair Skills Training for People with ARSACS and DM1 [NA]
Clinical trial from Laval University on wheelchair mobility and manual wheelchair skills training for people with ARSACS and Myotonic Dystro…
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CLINICAL_TRIALS trial_result · 2024-07-05Clinical Trial Update: Trial Readiness and Endpoint Assessment in Congenital and Childhood Myotonic Dystrophy
Completed clinical trial update focusing on trial readiness and endpoint assessment in congenital and childhood myotonic dystrophy.