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CLINICAL_TRIALS research · 2025-06-11

Clinical Trial Update: DMCRN-02-001: Assessing Pediatric Endpoints in DM1

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Summary

A clinical trial (DMCRN-02-001) assessing pediatric endpoints in congenital myotonic dystrophy (DM1) is currently recruiting.

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Diseases / indications

Snippet

Sponsor: Virginia Commonwealth University | Conditions: Congenital Myotonic Dystrophy, CDM | Status: RECRUITING