CLINICAL_TRIALS
research
· 2025-06-11
Clinical Trial Update: DMCRN-02-001: Assessing Pediatric Endpoints in DM1
Summary
A clinical trial (DMCRN-02-001) assessing pediatric endpoints in congenital myotonic dystrophy (DM1) is currently recruiting.
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Diseases / indications
Snippet
Sponsor: Virginia Commonwealth University | Conditions: Congenital Myotonic Dystrophy, CDM | Status: RECRUITING