Mucopolysaccharidosis Type Iva

• CLINICAL_TRIALS trial_result · 2018-04-11
  Clinical Trial Update: Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)

  A completed MAPLE study reports longitudinal findings on the psychological effects of enzyme replacement therapy in Morquio A syndrome (MPS …

• CLINICAL_TRIALS trial_result · 2016-02-01
  Clinical Trial Update: Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome [Phase 2]

  Phase 2 safety study of two doses of BMN 110 for Morquio A Syndrome has been terminated with results posted.

• CLINICAL_TRIALS trial_result · 2014-12-08
  Clinical Trial Update: A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

  This clinical trial update indicates that a BioMarin-sponsored study assessing subjects with Morquio syndrome (MPS IVA) has been terminated.

• CLINICAL_TRIALS trial_result · 2014-06-30
  Clinical Trial Update: A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA [Phase 1, Phase 2]

  Phase 1/2 study evaluating safety, tolerability and efficacy of BMN-110 in people with Mucopolysaccharidosis type IVA (Morquio A) with resul…

• CLINICAL_TRIALS trial_result · 2014-04-15
  Clinical Trial Update: A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) [Phase 3]

  Phase 3 double-blind study evaluating BMN 110 in Morquio A syndrome (MPS IVA); the trial is completed and results were posted in 2014.

• Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
• CLINICAL_TRIALS trial_result · 2008-10-20
  Clinical Trial Update: Morquio's Syndrome: a Case Study [Phase 4]

  Phase 4 clinical trial update for Morquio's disease (Mucopolysaccharidosis types IVA and IVB) has been terminated; the case study was sponso…