Clinical Trial Update: Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)

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Summary

A completed MAPLE study reports longitudinal findings on the psychological effects of enzyme replacement therapy in Morquio A syndrome (MPS IVA).

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Diseases / indications

• Morquio Syndrome
• Mucopolysaccharidosis Type Iva

Drugs mentioned

• VIMIZIM (Elosulfase alfa)

Snippet

Sponsor: Nadia Ali, PhD | Conditions: Morquio A Syndrome, Mucopolysaccharidosis IV A | Status: COMPLETED