Mucopolysaccharidosis Type Iva
📧 Sign up to get email alerts when something new happens for Mucopolysaccharidosis Type Iva.
Sign up freeTop drugs studied for this disease
-
FDA label_change · 2025-10-30FDA Approved: VIMIZIM — Supplemental Application (BioMarin Pharmaceutical Inc.)
The FDA approved a supplemental application for VIMIZIM (elosulfase alfa) from BioMarin Pharmaceutical, updating its labeling.