Mucopolysaccharidosis
📧 Sign up to get email alerts when something new happens for Mucopolysaccharidosis.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-03-04Clinical Trial Update: Physical Activity Intervention for MPS
Brunel University is planning a clinical trial to evaluate a physical activity intervention for mucopolysaccharidosis, which is currently no…
-
CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Mucopolysaccharidosis I (MPS I) Registry
This entry reports the completion of the Mucopolysaccharidosis I registry clinical trial sponsored by Genzyme. No specific results are provi…
-
CLINICAL_TRIALS research · 2025-08-22Clinical Trial Update: Nutritional Assessment in Patient of Mucopolysaccharide " [NA]
A clinical trial sponsored by Assiut University is evaluating nutritional assessment in patients with Mucopolysaccharidosis, focusing on mal…
-
CLINICAL_TRIALS research · 2024-07-03Clinical Trial Update: Long Term Follow-Up for RGX-111
This entry reports a long-term follow-up study for RGX-111 in mucopolysaccharidosis type I and indicates ongoing enrollment by invitation.
-
CLINICAL_TRIALS research · 2013-05-24Clinical Trial Update: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics
Clinical trial update indicating termination of a study designed to detect unrecognized mucopolysaccharidoses in children at rheumatology, h…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2013-03-01Clinical Trial Update: Non-invasive Assessment of Intraocular Pressure in MPS by Use of the Ocular Response Analyzer.
This clinical trial update describes a non-invasive method to assess intraocular pressure in patients with Mucopolysaccharidosis using the O…