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CLINICAL_TRIALS research · 2024-07-03

Clinical Trial Update: Long Term Follow-Up for RGX-111

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Summary

This entry reports a long-term follow-up study for RGX-111 in mucopolysaccharidosis type I and indicates ongoing enrollment by invitation.

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Diseases / indications

Drugs mentioned

  • RGX-111

Snippet

Sponsor: REGENXBIO Inc. | Conditions: Mucopolysaccharidosis I | Status: ENROLLING_BY_INVITATION