Mucopolysaccharidosis

Top drugs studied for this disease

All Approvals Safety alerts Label changes Trial results Research Guidance Withdrawals

CLINICAL_TRIALS withdrawal · 2025-12-09
Clinical Trial Update: A Study of ELAPRASE in Treatment-naïve Participants With Hunter Syndrome (Mucopolysaccharidosis [MPS] II) [Phase 4]
A Phase 4 trial of Elaprase (idursulfase) in treatment-naïve patients with Hunter syndrome has been withdrawn.