Mitochondrial Myopathies
📧 Sign up to get email alerts when something new happens for Mitochondrial Myopathies.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-02-18Clinical Trial Update: Validation of Oxygen Nanosensor in Mitochondrial Myopathy [Phase 1]
A Phase 1 clinical trial is underway to validate an oxygen nanosensor for use in mitochondrial myopathies and related mitochondrial diseases…
-
CLINICAL_TRIALS research · 2026-02-17Clinical Trial Update: Validation of Nanosensor Oxygen Measurement [Phase 1]
This is an update on a Phase 1 clinical trial to validate a nanosensor-based oxygen measurement method. The study, sponsored by Children's H…
-
CLINICAL_TRIALS research · 2025-11-10Clinical Trial Update: Applying pGz in Mitochondrial Disease [Phase 1]
A Phase 1 clinical trial conducted by Children’s Hospital of Philadelphia is recruiting to evaluate pGz in mitochondrial diseases, including…
-
CLINICAL_TRIALS trial_result · 2025-10-24Clinical Trial Update: Study to Evaluate Efficacy and Safety of Elamipretide in Subjects With Primary Mitochondrial Disease From Nuclear DNA Mutations (nPMD) [Phase 3]
Phase 3 study evaluating the efficacy and safety of elamipretide in subjects with primary mitochondrial disease from nuclear DNA mutations h…
-
CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: Natural History in Primary Mitochondrial Myopathies
A study to characterize the natural history of primary mitochondrial myopathies; recruitment is currently ongoing.
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2025-07-28Clinical Trial Update: Doxecitin and Doxribthymine in Adult Subjects With Thymidine Kinase 2 (TK2) Deficiency [Phase 2]
Phase 2 clinical trial update on Doxecitin and Doxribthymine for adults with thymidine kinase 2 deficiency–related mitochondrial myopathies,…
-
CLINICAL_TRIALS trial_result · 2024-11-29Clinical Trial Update: Promoting Resilience in Stress Management (PRISM) and Clinical-focused Narrative (CFN) Pilot in Adults With Primary Mitochondrial Disease (PMD). [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating resilience-based interventions (PRISM) and narrative-focused care (CFN) in adults with primary mitocho…
-
CLINICAL_TRIALS trial_result · 2024-06-12Clinical Trial Update: Genomic Profiling of Mitochondrial Disease - Imaging Analysis for Precise Mitochondrial Medicine
A completed Mayo Clinic study reports on genomic profiling and imaging analysis to advance precision mitochondrial medicine.
-
CLINICAL_TRIALS trial_result · 2022-08-31Clinical Trial Update: The KHENERGYZE Study [Phase 2]
Phase 2 trial update for the KHENERGYZE study investigating a treatment for mitochondrial diseases and mitochondrial myopathies (including M…
-
CLINICAL_TRIALS trial_result · 2018-02-23Clinical Trial Update: The KHENERGY Study [Phase 2]
Phase 2 trial update for the KHENERGY study in mitochondrial diseases has completed.
-
CLINICAL_TRIALS trial_result · 2016-04-06Clinical Trial Update: Nutritional Assessment in Mitochondrial Cytopathy
A completed clinical trial assessing nutritional status in mitochondrial cytopathy, conducted by Insel Gruppe AG and University Hospital Ber…