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CLINICAL_TRIALS research · 2025-11-10

Clinical Trial Update: Applying pGz in Mitochondrial Disease [Phase 1]

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Summary

A Phase 1 clinical trial conducted by Children’s Hospital of Philadelphia is recruiting to evaluate pGz in mitochondrial diseases, including mitochondrial myopa…

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Diseases / indications

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Sponsor: Children's Hospital of Philadelphia | Conditions: Mitochondrial Myopathies, Mitochondrial Diseases | Phase 1 | Status: RECRUITING