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CLINICAL_TRIALS trial_result · 2025-10-24

Clinical Trial Update: Study to Evaluate Efficacy and Safety of Elamipretide in Subjects With Primary Mitochondrial Disease From Nuclear DNA Mutations (nPMD) [Phase 3]

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Summary

Phase 3 study evaluating the efficacy and safety of elamipretide in subjects with primary mitochondrial disease from nuclear DNA mutations has completed.

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Diseases / indications

Drugs mentioned

  • Elamipretide (elamipretide)

Snippet

Sponsor: Stealth BioTherapeutics Inc. | Conditions: Mitochondrial Myopathies, Mitochondrial Pathology | Phase 3 | Status: COMPLETED