Long-chain Fatty Acid Oxidation Disorders
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CLINICAL_TRIALS trial_result · 2026-03-06Clinical Trial Update: Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program
The update indicates Ultragenyx's in-clinic disease monitoring program for long-chain fatty acid oxidation disorders is currently active but…
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CLINICAL_TRIALS trial_result · 2021-02-11Clinical Trial Update: A Study of UX007 (Triheptanoin) in Participants With Long-Chain Fatty Acid Oxidation Disorders (LC-FAOD) [Phase 2]
Phase 2 clinical trial evaluating UX007 (triheptanoin) in participants with long-chain fatty acid oxidation disorders (LC-FAOD) has complete…