Long-chain Fatty Acid Oxidation Disorders
📧 Sign up to get email alerts when something new happens for Long-chain Fatty Acid Oxidation Disorders.
Sign up freeTop drugs studied for this disease
-
FDA approval · 2023-10-30FDA Approved: DOJOLVI — Supplemental Application (Ultragenyx Pharmaceutical Inc.)
The FDA approved a supplemental application for DOJOLVI (triheptanoin) submitted by Ultragenyx Pharmaceutical Inc. The action pertains to it…
-
FDA approval · 2020-06-30FDA Approved: DOJOLVI — Original Application (Ultragenyx Pharmaceutical Inc.)
The FDA approved Dojolvi (triheptanoin) from Ultragenyx Pharmaceutical Inc. for the treatment of long-chain fatty acid oxidation disorders i…