Long-chain Fatty Acid Oxidation Disorders
📧 Sign up to get email alerts when something new happens for Long-chain Fatty Acid Oxidation Disorders.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: A Study to Determine the Effect of Triheptanoin Compared With Even-Chain MCT on MCEs in Pediatric Patients With LC-FAOD [Phase 3]
A Phase 3 clinical trial compares triheptanoin with even-chain medium-chain triglycerides to assess metabolic crisis events in pediatric pat…
-
CLINICAL_TRIALS research · 2024-08-23Clinical Trial Update: Exercise Intolerance Study in Long Chain Fatty Acid Oxidation Disorders
A clinical trial update announcing a recruiting study evaluating exercise intolerance in individuals with Long-chain Fatty Acid Oxidation Di…