Leigh Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: The NIH MINI Study: Metabolism, Infection, and Immunity in Inborn Errors of Metabolism
The NIH MINI study is currently recruiting to study metabolism, infection, and immunity in people with inborn errors of metabolism.
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CLINICAL_TRIALS research · 2026-03-31Clinical Trial Update: Sirolimus for Leigh Syndrome [Phase 2]
A Phase 2 clinical trial is investigating sirolimus for Leigh syndrome, with enrollment currently listed as enrolling by invitation.
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CLINICAL_TRIALS research · 2026-01-07Clinical Trial Update: Tissue Sample Study for Mitochondrial Disorders
Columbia University is enrolling by invitation in a tissue-sample study for mitochondrial disorders, including MELAS, Kearns-Sayre syndrome,…
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CLINICAL_TRIALS research · 2025-07-11Clinical Trial Update: A Dose-ranging Study of TTI-0102 in Adults and Children With Leigh Syndrome Spectrum (LSS) [Phase 2]
A Phase 2 dose-ranging clinical trial of TTI-0102 in adults and children with Leigh syndrome spectrum is listed as not yet recruiting.
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CLINICAL_TRIALS research · 2025-06-05Clinical Trial Update: Global Registry and Natural History Study for Mitochondrial Disorders
LMU Klinikum is conducting a global registry and natural history study to collect data on mitochondrial disorders, and the study is currentl…
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CLINICAL_TRIALS research · 2025-05-13Clinical Trial Update: Drug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural Cells
Clinical trial investigating repurposed drugs for Leigh syndrome using induced pluripotent stem cell derived neural cells; currently recruit…