CLINICAL_TRIALS
research
· 2025-05-13
Clinical Trial Update: Drug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural Cells
Summary
Clinical trial investigating repurposed drugs for Leigh syndrome using induced pluripotent stem cell derived neural cells; currently recruiting.
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Diseases / indications
Snippet
Sponsor: Charite University, Berlin, Germany | Conditions: Leigh Syndrome (Maternally Inherited, MILS), Leigh Syndrome (AR, AD, XR) | Status: RECRUITING