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CLINICAL_TRIALS research · 2026-03-31

Clinical Trial Update: Sirolimus for Leigh Syndrome [Phase 2]

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Summary

A Phase 2 clinical trial is investigating sirolimus for Leigh syndrome, with enrollment currently listed as enrolling by invitation.

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Diseases / indications

Drugs mentioned

  • Rapamune (sirolimus)

Snippet

Sponsor: Matthew Demczko | Conditions: Leigh Syndrome | Phase 2 | Status: ENROLLING_BY_INVITATION