CLINICAL_TRIALS
research
· 2026-03-31
Clinical Trial Update: Sirolimus for Leigh Syndrome [Phase 2]
Summary
A Phase 2 clinical trial is investigating sirolimus for Leigh syndrome, with enrollment currently listed as enrolling by invitation.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Matthew Demczko | Conditions: Leigh Syndrome | Phase 2 | Status: ENROLLING_BY_INVITATION