Juvenile Neuronal Ceroid Lipofuscinosis
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CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Investigations of Juvenile Neuronal Ceroid Lipofuscinosis
This ClinicalTrials.gov entry reports on ongoing investigations into juvenile neuronal ceroid lipofuscinosis (Batten disease), with the stud…
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CLINICAL_TRIALS research · 2025-05-30Clinical Trial Update: Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3 [Phase 3]
Phase 3 clinical trial update on PLX-200 for Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) describing safety, tolerability, and efficacy; t…