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CLINICAL_TRIALS research · 2025-05-30

Clinical Trial Update: Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3 [Phase 3]

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Summary

Phase 3 clinical trial update on PLX-200 for Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) describing safety, tolerability, and efficacy; the study is not yet …

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Diseases / indications

Drugs mentioned

  • PLX-200 (PLX-200)

Snippet

Sponsor: Polaryx Therapeutics, Inc. | Conditions: Juvenile Neuronal Ceroid Lipofuscinosis | Phase 3 | Status: NOT_YET_RECRUITING