CLINICAL_TRIALS
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· 2025-05-30
Clinical Trial Update: Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3 [Phase 3]
Summary
Phase 3 clinical trial update on PLX-200 for Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) describing safety, tolerability, and efficacy; the study is not yet …
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Sponsor: Polaryx Therapeutics, Inc. | Conditions: Juvenile Neuronal Ceroid Lipofuscinosis | Phase 3 | Status: NOT_YET_RECRUITING