Juvenile Neuronal Ceroid Lipofuscinosis
📧 Sign up to get email alerts when something new happens for Juvenile Neuronal Ceroid Lipofuscinosis.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Functional Near-Infrared Spectroscopy (fNIRS) Combined With Diffuse Correlation Spectroscopy (DCS) in Neurocognitive Disease as Compared to Healthy Neurotypical Controls
Status update on a completed clinical trial evaluating functional near-infrared spectroscopy combined with diffuse correlation spectroscopy …
-
CLINICAL_TRIALS research · 2026-02-24Clinical Trial Update: Investigations of Juvenile Neuronal Ceroid Lipofuscinosis
This ClinicalTrials.gov entry reports on ongoing investigations into juvenile neuronal ceroid lipofuscinosis (Batten disease), with the stud…
-
CLINICAL_TRIALS research · 2025-05-30Clinical Trial Update: Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3 [Phase 3]
Phase 3 clinical trial update on PLX-200 for Juvenile Neuronal Ceroid Lipofuscinosis (CLN3) describing safety, tolerability, and efficacy; t…
-
CLINICAL_TRIALS trial_result · 2017-01-23Clinical Trial Update: Cellcept for Treatment of Juvenile Neuronal Ceroid Lipofuscinosis [Phase 2]
Phase 2 clinical trial of Cellcept for Juvenile Neuronal Ceroid Lipofuscinosis has completed with results posted.