Hereditary Tyrosinemia Type
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care
A long-term safety study of Orfadin (nitisinone) in patients with hereditary tyrosinemia type I in standard clinical care has completed.
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CLINICAL_TRIALS trial_result · 2016-12-13Clinical Trial Update: Bioavailability Food-Effect Study of an Oral Nitisinone Formulation to Treat Hereditary Tyrosinemia (HT-1) [Phase 1]
Phase 1 bioavailability/food-effect study of an oral nitisinone formulation for Hereditary Tyrosinemia Type I completed with results posted.
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CLINICAL_TRIALS trial_result · 2016-12-13Clinical Trial Update: Bioequivalence Study of Two Nitisinone Formulations Compared to Orfadin [Phase 1]
A Phase 1 bioequivalence trial compared two nitisinone formulations to Orfadin for hereditary tyrosinemia type I; the study is completed and…
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CLINICAL_TRIALS trial_result · 2016-10-17Clinical Trial Update: Bioequivalence Study of Two Oral Nitisinone Formulations to Treat Hereditary Tyrosinemia (HT-1) [Phase 1]
A Phase 1 study comparing two oral formulations of nitisinone for hereditary tyrosinemia type I completed, with bioequivalence results poste…
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CLINICAL_TRIALS trial_result · 2015-11-11Clinical Trial Update: Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 [Phase 3]
A Phase 3 trial comparing once-daily versus twice-daily dosing of nitisinone in Hereditary Tyrosinemia Type I has completed.
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CLINICAL_TRIALS trial_result · 2014-03-04Clinical Trial Update: Taste and Palatability of Orfadin Suspension [Phase 1]
This Phase 1 study evaluated the taste and palatability of Orfadin suspension in patients with hereditary tyrosinemia type I, with results p…
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CLINICAL_TRIALS trial_result · 2014-02-20Clinical Trial Update: Bioequivalence of Orfadin Suspension Compared to Orfadin Capsules, and the Effect of Food on the Bioavailability of the Suspension [Phase 1]
A Phase 1 study in healthy volunteers evaluated the bioequivalence of Orfadin suspension to Orfadin capsules and the effect of food on suspe…