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CLINICAL_TRIALS trial_result · 2024-09-19

Clinical Trial Update: Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care

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Summary

A long-term safety study of Orfadin (nitisinone) in patients with hereditary tyrosinemia type I in standard clinical care has completed.

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Diseases / indications

Drugs mentioned

  • Orfadin (nitisinone)

Snippet

Sponsor: Swedish Orphan Biovitrum | Conditions: Hereditary Tyrosinemia, Type I | Status: COMPLETED