CLINICAL_TRIALS
trial_result
· 2024-09-19
Clinical Trial Update: Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care
Summary
A long-term safety study of Orfadin (nitisinone) in patients with hereditary tyrosinemia type I in standard clinical care has completed.
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Diseases / indications
Drugs mentioned
Snippet
Sponsor: Swedish Orphan Biovitrum | Conditions: Hereditary Tyrosinemia, Type I | Status: COMPLETED