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CLINICAL_TRIALS trial_result · 2015-11-11

Clinical Trial Update: Efficacy and Safety of Once Daily Dosing Compared to Twice Daily Dosing of Nitisinone in HT-1 [Phase 3]

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Summary

A Phase 3 trial comparing once-daily versus twice-daily dosing of nitisinone in Hereditary Tyrosinemia Type I has completed.

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Diseases / indications

Drugs mentioned

  • Nitisinone (Nitisinone)

Snippet

Sponsor: Swedish Orphan Biovitrum | Conditions: Hereditary Tyrosinemia, Type I | Phase 3 | Status: COMPLETED