Hemophilia
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CLINICAL_TRIALS trial_result · 2025-02-07Clinical Trial Update: Hemophilia Non-Interventional Study Prior to SerpinPC Intervention (PRESent-5)
A non-interventional study in Hemophilia A and Hemophilia B evaluating eligibility before SerpinPC treatment has been terminated.
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CLINICAL_TRIALS trial_result · 2025-02-06Clinical Trial Update: The Safety and Tolerability of SerpinPC in Healthy Men and in Men with Severe Blood Disorders (haemophilia a and B) [Phase 1, Phase 2]
The trial update reports on the safety and tolerability of SerpinPC in healthy men and in men with Hemophilia A or B across Phase 1 and Phas…
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CLINICAL_TRIALS trial_result · 2025-02-04Clinical Trial Update: ADYNOVATE Drug Use-Results Survey
Takeda released results from a Hemophilia A drug-use survey of ADYNOVATE. The results were posted on February 4, 2025.
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CLINICAL_TRIALS trial_result · 2025-01-22Clinical Trial Update: Safety and Efficacy of STSP-0601 in Adult Patients with Hemophilia a or B with Inhibitor [Phase 2]
A Phase 2 study evaluating the safety and efficacy of STSP-0601 in adults with Hemophilia A or B with inhibitors has completed.
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CLINICAL_TRIALS trial_result · 2025-01-20Clinical Trial Update: Factor IX as Adjunctive Therapy to Emicizumab (EMIX) [EARLY_Phase 1]
This is an early Phase 1 study evaluating Factor IX as adjunctive therapy to Emicizumab (EMIX) for Hemophilia A. The trial status shows comp…
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CLINICAL_TRIALS trial_result · 2025-01-16Clinical Trial Update: An 18-month Low-interventional Study to Assess Joint Health in Haemophilia A and B Patients on Prophylaxis With Efmoroctocog Alfa or Eftrenonacog Alfa [Phase 4]
This update reports the termination of an 18-month Phase 4 study evaluating joint health in haemophilia A and B patients on prophylaxis with…
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CLINICAL_TRIALS trial_result · 2025-01-13Clinical Trial Update: EVALUATION of the OVERALL HAEMOSTATIC CAPACITY of MIM8 with GLOBAL HAEMOSTASIS ASSAYS and FIBRIN CLOT ULTRASTRUCTURE
A completed clinical trial evaluating the overall haemostatic capacity of MIM8 using global haemostasis assays and fibrin clot ultrastructur…
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CLINICAL_TRIALS trial_result · 2024-12-30Clinical Trial Update: A Gene Transfer Study for Hemophilia A [Phase 1, Phase 2]
Clinical trial update for a gene transfer therapy in Hemophilia A (Phase 1/2) with completed status and results posted.
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CLINICAL_TRIALS trial_result · 2024-12-30Clinical Trial Update: KN057 Multiple Dose Study in Moderately Severe to Severe Hemophilia [Phase 2]
A Phase 2 multiple-dose study of KN057 in moderately severe to severe hemophilia has completed, with the update noting trial status rather t…
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CLINICAL_TRIALS trial_result · 2024-11-29Clinical Trial Update: Long-Term Safety and Efficacy of Spark-Sponsored Gene Therapies in Males With Hemophilia A
This update summarizes long-term safety and efficacy data from Spark Therapeutics–sponsored gene therapies studied in males with Hemophilia …
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CLINICAL_TRIALS trial_result · 2024-11-27Clinical Trial Update: In Vitro Correction of Thrombin Generation by Concizumab (Anti-TFPI) for Severe Hemophilia Patients
This completed trial update reports in vitro evidence that concizumab (an anti-TFPI antibody) corrected thrombin generation in samples from …
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CLINICAL_TRIALS trial_result · 2024-11-15Clinical Trial Update: A Study of TAK-660 in Surgical Procedures for People With Hemophilia A.
TAK-660 has completed a study evaluating its use in surgical procedures for people with Hemophilia A, with results posted on 2024-11-15.
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CLINICAL_TRIALS trial_result · 2024-10-29Clinical Trial Update: Case and Use Scenario Study to Gain Knowledge on the User Needs for a Medical Device for Hemophilia a Monitoring
This completed clinical trial conducted case and use scenario studies to gather insights on user needs for a medical device intended to moni…
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CLINICAL_TRIALS trial_result · 2024-10-21Clinical Trial Update: Effect of Kinetic Chain Exercises on Muscle Strength, Joint Position Sense and Quality of Life in Children with Haemophilia. [NA]
A clinical trial investigating how kinetic chain exercises affect muscle strength, joint position sense, and quality of life in children wit…
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CLINICAL_TRIALS trial_result · 2024-10-02Clinical Trial Update: Prospective, Non-interventional Study to Evaluate the Effectiveness of Elocta Compared to Conventional Factor Products
A completed non-interventional study comparing the effectiveness of Elocta with conventional factor VIII products in individuals with Hemoph…
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CLINICAL_TRIALS trial_result · 2024-09-27Clinical Trial Update: Study of TU7710 in Warfarin Anti-coagulated Healthy Male Subjects [Phase 1]
Phase 1 study evaluating TU7710 in warfarin-anticoagulated healthy male subjects; conditions listed include Hemophilia A and Hemophilia B.
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: A Safety and Efficacy Study of STSP-0601 in Adult Patients With Hemophilia A or B With Inhibitor [Phase 1, Phase 2]
Phase 1/2 safety and efficacy study of STSP-0601 in adult patients with Hemophilia A or B with inhibitors has been completed.
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: A Safety Study of STSP-0601 in Adult Patients With Hemophilia A or B With Inhibitor [Phase 1]
Phase 1 safety study of STSP-0601 in adults with Hemophilia A or Hemophilia B with inhibitors has completed.
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Psychometric Validation of the Hemophilia Functional Ability Scoring Tool (Hemo-FAST)
Psychometric validation results for the Hemophilia Functional Ability Scoring Tool (Hemo-FAST) are reported for patients with Hemophilia A a…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: A Study to Evaluate the Real-world Effectiveness and Usage of Alprolix in Patients With Haemophilia B in France
This completed clinical trial evaluated the real-world effectiveness and usage of Alprolix in patients with Hemophilia B in France.
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: Impact on French Physician's Haemophilia Treatment Management Decision Based on Systematic Joint Examination [NA]
This entry reports the completion of NCT04133883, a trial assessing how systematic joint examination influences French physicians' managemen…
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CLINICAL_TRIALS trial_result · 2024-09-04Clinical Trial Update: Safety & Efficacy of Encapsulated Allogeneic FVIII Cell Therapy in Haemophilia A [Phase 1, Phase 2]
Phase 1/2 trial evaluating an encapsulated allogeneic FVIII cell therapy for Hemophilia A was terminated, with results posted in September 2…
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CLINICAL_TRIALS trial_result · 2024-08-13Clinical Trial Update: Vitamin D Deficiency and Body Composition in the Patients With Hemophilia
A completed clinical study evaluating vitamin D deficiency and body composition in patients with hemophilia, including relationships to sarc…
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CLINICAL_TRIALS trial_result · 2024-08-09Clinical Trial Update: Immune Tolerance Induction in Haemophilia A Patients Using Wilate or Nuwiq
The trial evaluating immune tolerance induction in Hemophilia A patients using Wilate or Nuwiq has been terminated, with results posted on 2…
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CLINICAL_TRIALS trial_result · 2024-07-22Clinical Trial Update: RIXUBIS Drug Use-Result Survey (Japan)
A Japan drug-use survey for RIXUBIS in Hemophilia B with results posted.