Hemophilia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-08-17Clinical Trial Update: Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults [Phase 3]
Pfizer is evaluating the efficacy and safety of giroctocogene fitelparvovec (PF-07055480) gene therapy in adults with moderately severe to s…
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CLINICAL_TRIALS trial_result · 2025-08-17Clinical Trial Update: Study to Evaluate the Efficacy and Safety of PF-07055480 / Giroctocogene Fitelparvovec Gene Therapy in Moderately Severe to Severe Hemophilia A Adults [Phase 3]
Phase 3 trial update for PF-07055480 Giroctocogene fitelparvovec gene therapy in adults with moderately severe to severe Hemophilia A.
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CLINICAL_TRIALS trial_result · 2025-08-12Clinical Trial Update: Effects of Ultrasound and Infrared on Joint Pain and Movement in Hemophilia A Patients. [NA]
This completed clinical trial evaluated whether ultrasound and infrared therapy can reduce joint pain and improve movement in people with He…
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CLINICAL_TRIALS trial_result · 2025-08-08Clinical Trial Update: Fitusiran Prophylaxis in Male Pediatric Subjects Aged 1 to Less Than 12 Years With Hemophilia A or B [Phase 3]
Phase 3 trial status update for Fitusiran prophylaxis in male pediatric patients aged 1 to less than 12 years with Hemophilia A or B; the st…
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CLINICAL_TRIALS trial_result · 2025-08-01Clinical Trial Update: Long-term Safety and Efficacy of Efanesoctocog Alfa (BIVV001) in Previously Treated Patients With Hemophilia A [Phase 3]
Phase 3 study update reporting long-term safety and efficacy of efanesoctocog alfa (BIVV001) in previously treated patients with Hemophilia …
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CLINICAL_TRIALS trial_result · 2025-07-28Clinical Trial Update: A Study of PEGylated Recombinant Factor VIII (BAX855) in Previously Untreated Young Children With Severe Hemophilia A [Phase 3]
A Phase 3 study evaluating PEGylated recombinant Factor VIII (BAX855) in previously untreated young children with severe Hemophilia A has co…
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CLINICAL_TRIALS trial_result · 2025-07-24Clinical Trial Update: A Study to Learn How Safe the Study Treatment BAY94-9027 is and How it Affects the Body in Previously Treated Children Aged 7 to Less Than 12 Years With Severe Hemophilia A, a Genetic Bleeding Disorder That is Caused by the Lack of a Protein Called Clotting Factor 8 (FVIII) in the Blood [Phase 3]
Phase 3 trial assessing the safety and pharmacodynamic effects of BAY94-9027 in previously treated children aged 7 to less than 12 with seve…
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CLINICAL_TRIALS trial_result · 2025-07-09Clinical Trial Update: A Phase 3 Study of the Safety and Efficacy of Coagulation Factor VIIa (Recombinant) for the Prevention of Excessive Bleeding in Patients With Congenital Hemophilia A or B With Inhibitors to Factor VIII or IX Undergoing Elective Major Surgical Procedures SCOPE HIM [Phase 3]
A Phase 3 trial evaluating recombinant factor VIIa to prevent excessive bleeding in patients with congenital Hemophilia A or B with inhibito…
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CLINICAL_TRIALS trial_result · 2025-06-25Clinical Trial Update: Comparison of Efficiency of Closed Kinetic Chain Exercises Versus Proprioceptive Exercises Patient With Hemophilia [NA]
This update describes a completed clinical trial comparing closed kinetic chain exercises with proprioceptive exercises in people with Hemop…
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CLINICAL_TRIALS trial_result · 2025-06-15Clinical Trial Update: Study to Learn More About the Physical Activity Level of Patients Suffering From Hemophilia A Treated With Damoctocog Alfa Pegol (LIFE ACTIVE Study)
The LIFE ACTIVE study evaluating physical activity levels in patients with Hemophilia A treated with damoctocog alfa pegol has completed.
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CLINICAL_TRIALS trial_result · 2025-06-10Clinical Trial Update: Study of the Efficacy and Safety PF-06741086 in Adult and Teenage Participants With Severe Hemophilia A or Moderately Severe to Severe Hemophilia B [Phase 3]
This document reports the completion of a Phase 3 trial evaluating the efficacy and safety of PF-06741086 in adults and teens with Hemophili…
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CLINICAL_TRIALS trial_result · 2025-06-05Clinical Trial Update: A Proof-of-concept Study to Reduce Treatment Burden in Haemophilia Participants Receiving Factor VIII and Factor IX Infusions [NA]
This clinical trial update reports a proof-of-concept study aimed at reducing treatment burden for people with hemophilia who receive Factor…
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CLINICAL_TRIALS trial_result · 2025-05-31Clinical Trial Update: A Research Study Investigating Nonacog Beta Pegol (N9-GP) for Treatment and Prevention of Bleedings in Chinese People With Haemophilia B [Phase 3]
Phase 3 trial of Nonacog Beta Pegol (N9-GP) in Chinese patients with Hemophilia B has completed, with results posted for evaluating treatmen…
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CLINICAL_TRIALS trial_result · 2025-05-01Clinical Trial Update: A Study of Adynovate in Previously Treated Chinese Teenagers and Adults With Severe Hemophilia A [Phase 3]
A Phase 3 trial of Adynovate in previously treated Chinese teenagers and adults with severe Hemophilia A has completed, and the trial result…
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CLINICAL_TRIALS trial_result · 2025-04-30Clinical Trial Update: The Dynamic Interplay Between Bleeding Phenotype and Baseline Factor Level in Moderate and Mild Hemophilia A and B
Document summarizing a completed AMC-UvA-sponsored trial that investigates how baseline factor levels relate to bleeding phenotype in indivi…
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CLINICAL_TRIALS trial_result · 2025-04-30Clinical Trial Update: Kinesiophobia in the Parents of Hemophilia Patients
A completed clinical trial evaluating kinesiophobia in the parents of patients with hemophilia and hemophilic arthropathy.
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CLINICAL_TRIALS trial_result · 2025-04-27Clinical Trial Update: Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia With Inhibitors [Phase 3]
Phase 3 trial update for Concizumab in people with hemophilia A or B with inhibitors; results have been posted.
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CLINICAL_TRIALS trial_result · 2025-04-24Clinical Trial Update: A Trial of the Safety and Efficacy of Single-Dose Administration of ANB-010 in Subjects With Hemophilia A [Phase 1, Phase 2]
Biocad reports on a Phase 1/2 study evaluating a single-dose administration of ANB-010 for Hemophilia A. The trial is currently active but n…
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CLINICAL_TRIALS trial_result · 2025-04-18Clinical Trial Update: A Post Approval Commitment Study to Gain More Information on How Safe and Effective KOVALTRY is in Chinese Children, Adolescents /Adults With Severe Hemophilia A [Phase 4]
A Phase 4 post-approval study by Bayer evaluating safety and effectiveness of Kovaltry (octocog alfa) in Chinese children, adolescents, and …
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CLINICAL_TRIALS trial_result · 2025-03-11Clinical Trial Update: The Efficacy and Safety of SerpinPC in Participants with Severe Hemophilia a or Moderately Severe to Severe Hemophilia B [Phase 2]
Phase 2 trial evaluating the efficacy and safety of SerpinPC in participants with severe Hemophilia A or moderately severe to severe Hemophi…
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: Gene Therapy for Chinese Hemophilia B [NA]
A completed clinical trial in China studied a gene therapy approach for Hemophilia B.
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CLINICAL_TRIALS trial_result · 2025-02-21Clinical Trial Update: The Efficacy and Safety of ZS802 in Chinese Hemophilia A Patients. [NA]
This clinical trial update reports on the efficacy and safety of ZS802 for Hemophilia A in Chinese patients; the study is currently recruiti…
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CLINICAL_TRIALS trial_result · 2025-02-13Clinical Trial Update: Safety and Pharmacokinetics of Subcutaneous Injection of OCTA101 in Adult Patients With Severe Hemophilia A [Phase 1, Phase 2]
Phase 1/2 trial evaluating safety and pharmacokinetics of subcutaneous OCTA101 in adults with Hemophilia A; the study was terminated but res…
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CLINICAL_TRIALS trial_result · 2025-02-12Clinical Trial Update: ATHN 7: Hemophilia Natural History Study
ATHN 7 is a natural history study of hemophilia patients conducted by the American Thrombosis and Hemostasis Network, and this update notes …
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CLINICAL_TRIALS trial_result · 2025-02-10Clinical Trial Update: The Long-term Safety and Efficacy of SerpinPC in Subjects with Hemophilia Who Completed a Sponsored SerpinPC Clinical Trial [Phase 3]
This clinical trial update covers the long-term safety and efficacy of SerpinPC in people with Hemophilia A or Hemophilia B who completed pr…