Hemophilia
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CLINICAL_TRIALS trial_result · 2026-02-03Clinical Trial Update: Resistance Training With Blood Flow Restriction in Hemophilia [NA]
This ClinicalTrials.gov update reports the completion of a study evaluating resistance training with blood flow restriction in people with h…
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CLINICAL_TRIALS trial_result · 2026-01-26Clinical Trial Update: A Study to Evaluate Overall Health, Physical Activity, and Joint Outcomes in Participants With Severe or Moderate Hemophilia A Without Factor VIII Inhibitors on Emicizumab Prophylaxis [Phase 4]
A Phase 4 clinical trial update describing a study to evaluate overall health, physical activity, and joint outcomes in people with Hemophil…
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CLINICAL_TRIALS trial_result · 2026-01-20Clinical Trial Update: Goal Attainment and Physical Activity in People With Hemophilia A
This clinical trial update reports the termination of a Sanofi-sponsored study examining goal attainment and physical activity in people wit…
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CLINICAL_TRIALS trial_result · 2026-01-14Clinical Trial Update: Physiotherapy to Improve Balance and Walking Capacity in Hemophilia [NA]
A completed clinical trial evaluating physiotherapy to improve balance and walking capacity in people with hemophilia.
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CLINICAL_TRIALS trial_result · 2026-01-13Clinical Trial Update: Nuwiq Dosing and Outcomes In the ManagEment of Women/Girls With Haemophilia A Needing FVIII Treatment for Surgery [Phase 4]
This Phase 4 clinical trial update evaluates dosing of Nuwiq (octocog alfa) and related outcomes for surgical management in women and girls …
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CLINICAL_TRIALS trial_result · 2026-01-12Clinical Trial Update: A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)
Long-term follow-up study in severe Hemophilia A patients who previously received BMN 270; enrollment is by invitation.
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CLINICAL_TRIALS trial_result · 2025-12-08Clinical Trial Update: A Research Study Investigating Mim8 in Adults and Adolescents With Haemophilia A With or Without Inhibitors [Phase 3]
A Phase 3 study evaluating Mim8 in adults and adolescents with Hemophilia A, with or without inhibitors, has completed.
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CLINICAL_TRIALS trial_result · 2025-12-02Clinical Trial Update: Feasibility and Safety of Blood-Flow-Restriction Training in Patients With Hemophilia [NA]
A clinical trial is evaluating the feasibility and safety of blood-flow-restriction training in patients with hemophilia; the study is curre…
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CLINICAL_TRIALS trial_result · 2025-11-24Clinical Trial Update: A Phase 1b Study to Assess the Safety, Tolerability, PK and PD of MG1113 in Hemophilia Patient [Phase 1]
A Phase 1b trial evaluated MG1113 in hemophilia patients to assess safety, tolerability, pharmacokinetics and pharmacodynamics. The study ha…
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CLINICAL_TRIALS trial_result · 2025-11-24Clinical Trial Update: Balance Evaluation in Adult Hemophilia
A completed clinical trial evaluating balance and postural control in adults with hemophilia.
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CLINICAL_TRIALS trial_result · 2025-11-18Clinical Trial Update: MRI Role in Knee Hemophilic Arthopathy
A study from Assiut University is evaluating the role of MRI in knee hemophilic arthropathy and is not yet recruiting.
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CLINICAL_TRIALS trial_result · 2025-11-13Clinical Trial Update: A Research Study Looking at Mim8 in Children With Haemophilia A With or Without Inhibitors [Phase 3]
Phase 3 trial evaluating Mim8 in children with Hemophilia A, with or without inhibitors, has completed.
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CLINICAL_TRIALS trial_result · 2025-11-12Clinical Trial Update: Prophylaxis Regimen for Hemophilia A Patients [Phase 4]
Bayer reports completed Phase 4 results for a prophylaxis regimen in patients with Hemophilia A.
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CLINICAL_TRIALS trial_result · 2025-11-06Clinical Trial Update: A Study to Evaluate Prospective Efficacy and Safety Data of Current FIX Prophylaxis Replacement Therapy in Adult Hemophilia B Subjects (FIX:C≤2%) or Current FVIII Prophylaxis Replacement Therapy in Adult Hemophilia A Subjects (FVIII:C≤1%) [Phase 3]
Phase 3 trial evaluating the efficacy and safety of FIX prophylaxis for adult Hemophilia B and FVIII prophylaxis for adult Hemophilia A; the…
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CLINICAL_TRIALS trial_result · 2025-10-31Clinical Trial Update: Research Study to Look at How Well the Drug Concizumab Works in Your Body if You Have Haemophilia Without Inhibitors [Phase 3]
Phase 3 trial update evaluating concizumab in people with hemophilia without inhibitors; results have been posted.
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CLINICAL_TRIALS trial_result · 2025-10-24Clinical Trial Update: Nuwiq for Perioperative Management Of Patients With Haemophilia A on Emicizumab Regular Prophylaxis Study [Phase 4]
Phase 4 trial update evaluating Nuwiq (recombinant factor VIII) for perioperative management in patients with Hemophilia A on emicizumab pro…
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CLINICAL_TRIALS trial_result · 2025-10-23Clinical Trial Update: Drug Use Investigation of Kovaltry in Hemophilia A Patients
This document reports the completion of a drug-use investigation evaluating Kovaltry for Hemophilia A.
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CLINICAL_TRIALS trial_result · 2025-09-30Clinical Trial Update: A Study of Recombinant AAV2/6 Human Factor 8 Gene Therapy SB-525 (PF-07055480) in Subjects With Severe Hemophilia A [Phase 2]
Phase 2 study of the recombinant AAV2/6 factor VIII gene therapy SB-525 (PF-07055480) for severe hemophilia A has completed, with results po…
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CLINICAL_TRIALS trial_result · 2025-09-29Clinical Trial Update: An International Study to Evaluate the Real-world Effectiveness and Usage of Alprolix in Patients With Haemophilia B
This completed international trial evaluated the real-world effectiveness and usage of Alprolix in patients with Hemophilia B.
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CLINICAL_TRIALS trial_result · 2025-09-18Clinical Trial Update: Pharmacokinetic Assessment of Standard Half-Life (SHL) FVIII, Extended Half-Life (EHL) FVIII, and Efanesoctocog Alfa (BIVV001) in Severe Hemophilia A [Phase 1]
This Phase 1 trial assessed the pharmacokinetics of standard half-life FVIII, extended half-life FVIII, and efanesoctocog alfa (BIVV001) in …
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CLINICAL_TRIALS trial_result · 2025-09-17Clinical Trial Update: Efficacy and Safety of KN057 Prophylaxis in Patients With Haemophilia A or B With Inhibitors [Phase 3]
Phase 3 clinical trial update on KN057 for prophylaxis in patients with Hemophilia A or B with inhibitors; the study is currently active but…
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CLINICAL_TRIALS trial_result · 2025-09-11Clinical Trial Update: A Study of BAX 888 in Male Adults With Severe Hemophilia A [Phase 1, Phase 2]
Results from a Phase 1/2 study of BAX 888 in male adults with severe Hemophilia A have been posted.
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CLINICAL_TRIALS trial_result · 2025-09-10Clinical Trial Update: Comparison of Pulmonary Function, Exercise Capacity, and Physical Activity Level Between Children With Hemophilia and Healthy Controls
This clinical trial update compares pulmonary function, exercise capacity, and physical activity level between children with hemophilia and …
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CLINICAL_TRIALS trial_result · 2025-09-08Clinical Trial Update: Real World Use of Emicizumab in Infants and Children Ages 0-3 Years With Hemophilia A
A completed observational study evaluating real-world use of emicizumab in infants and young children aged 0-3 years with Hemophilia A, repo…
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CLINICAL_TRIALS trial_result · 2025-08-22Clinical Trial Update: Gene Therapy Study in Severe Hemophilia A Patients With Antibodies Against AAV5 [Phase 1, Phase 2]
BioMarin's Phase 1/2 gene therapy trial in severe Hemophilia A patients with antibodies against AAV5 was terminated and results have been po…