Clinical Trial Update: A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial evaluating the safety and effectiveness of REGV131-LNP1265, a coagulation factor IX gene insertion therapy, in pediatric to adult par…

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Diseases / indications

• Hemophilia

Drugs mentioned

• REGV131-LNP1265

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Hemophilia B | Phase 1, Phase 2 | Status: RECRUITING