Glycogen Storage Disease Type Ia
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CLINICAL_TRIALS trial_result · 2026-03-25Clinical Trial Update: A Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia (GSDIa) [Phase 3]
Phase 3 study of AAV8-mediated glucose-6-phosphatase gene transfer for Glycogen Storage Disease Type Ia has completed.
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CLINICAL_TRIALS trial_result · 2024-05-29Clinical Trial Update: Retrospective Study of Glucose Monitoring for Glycemic Control in Patients With GSDIa
A retrospective study evaluating glucose monitoring for glycemic control in patients with Glycogen Storage Disease Type Ia has completed. Sp…
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CLINICAL_TRIALS trial_result · 2022-11-18Clinical Trial Update: Safety and Dose-Finding Study of DTX401 (AAV8G6PC) in Adults With Glycogen Storage Disease Type Ia (GSDIa) [Phase 1, Phase 2]
Phase 1/2 safety and dose-finding clinical trial of DTX401 (AAV8G6PC) in adults with Glycogen Storage Disease Type Ia has completed with res…
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CLINICAL_TRIALS trial_result · 2022-02-11Clinical Trial Update: Endogenous Glucose Production in Patients With Glycogen Storage Disease Type Ia [Phase 1, Phase 2]
Phase 1/2 trial investigating endogenous glucose production in patients with Glycogen Storage Disease Type Ia has completed.