AAV8-G6PC gene therapy

Adeno-associated virus serotype 8-mediated glucose-6-phosphatase gene transfer · Ultragenyx Pharmaceutical Inc.

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1 regulatory and trial event tracked for AAV8-G6PC gene therapy, covering 2026-03-25 to 2026-03-25. Get the full timeline:

Most recent: Clinical Trial Update: A Study of Adeno-Associated Virus Serotype 8-Mediated Gene Transfer of Glucose-6-Phosphatase in Patients With Glycogen Storage Disease Type Ia (GSDIa) [Phase 3]

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