Clinical Trial Update: Safety and Dose-Finding Study of DTX401 (AAV8G6PC) in Adults With Glycogen Storage Disease Type Ia (GSDIa) [Phase 1, Phase 2]

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Summary

Phase 1/2 safety and dose-finding clinical trial of DTX401 (AAV8G6PC) in adults with Glycogen Storage Disease Type Ia has completed with results posted.

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Diseases / indications

• Glycogen Storage Disease Type Ia

Drugs mentioned

• AAV8G6PC
• DTX401

Snippet

Sponsor: Ultragenyx Pharmaceutical Inc | Conditions: GSD1 | Phase 1, Phase 2 | Status: COMPLETED | Results posted: 2022-11-18