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CLINICAL_TRIALS trial_result · 2025-10-30

Clinical Trial Update: A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia [Phase 3]

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Summary

Phase 3 study of Vatiquinone in Friedreich Ataxia is currently active but not recruiting.

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Diseases / indications

Drugs mentioned

  • Vatiquinone

Snippet

Sponsor: PTC Therapeutics | Conditions: Friedreich Ataxia | Phase 3 | Status: ACTIVE_NOT_RECRUITING