Duchenne Muscular Dystrophy
📧 Sign up to get email alerts when something new happens for Duchenne Muscular Dystrophy.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS research · 2026-04-06Clinical Trial Update: A Multicenter Cohort Study of Duchenne and Becker Muscular Dystrophy in Western Chinese Children
A multicenter cohort study protocol investigating Duchenne muscular dystrophy and Becker muscular dystrophy in Western Chinese children. The…
-
CLINICAL_TRIALS trial_result · 2026-04-03Clinical Trial Update: An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy [Phase 4]
Phase 4 open-label study of golodirsen in non-ambulant Duchenne muscular dystrophy patients has been terminated.
-
EMA approval · 2026-03-27EMA Authorised: Duvyzat (givinostat hydrochloride monohydrate) — Italfarmaco S.p.A.
The European Medicines Agency authorised Duvyzat, containing givinostat hydrochloride monohydrate, for Duchenne muscular dystrophy under a c…
-
CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: Long Term Follow-up for RGX-202
A clinical trial update on long-term follow-up for RGX-202 in Duchenne Muscular Dystrophy, with enrollment by invitation.
-
CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of Single Intravenous Infusion of JWK007 in Patients With Duchenne Muscular Dystrophy (DMD) [Phase 1]
Phase 1 clinical trial evaluating safety, tolerability, and initial efficacy of a single intravenous infusion of JWK007 in Duchenne Muscular…
- Want full summaries, importance scores, and drug timelines? Upgrade to Plus or Pro.
-
CLINICAL_TRIALS research · 2026-03-16Clinical Trial Update: A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular Dystrophy [NA]
A study is evaluating the safety and tolerability of Rituxan (rituximab) in Duchenne Muscular Dystrophy. The trial is not yet recruiting.
-
CLINICAL_TRIALS trial_result · 2026-03-13Clinical Trial Update: Twice Weekly Steroids and Exercise as Therapy for DMD [Phase 2]
A Phase 2 clinical trial evaluating twice-weekly steroids and exercise as therapy for Duchenne Muscular Dystrophy has completed, with result…
-
CLINICAL_TRIALS research · 2026-03-13Clinical Trial Update: PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD) [Phase 1, Phase 2]
Clinical trial update on PBGENE-DMD for Duchenne muscular dystrophy, outlining a Phase 1/2a safety and preliminary efficacy study that is no…
-
CLINICAL_TRIALS trial_result · 2026-03-10Clinical Trial Update: Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy [Phase 3]
Phase 3 trial update presenting long-term outcomes for ataluren in Duchenne muscular dystrophy; results were posted in March 2026.
-
CLINICAL_TRIALS research · 2026-03-10Clinical Trial Update: Duchenne Muscular Dystrophy Video Assessment Registry
This clinical trial update reports completion of the Duchenne Muscular Dystrophy Video Assessment Registry and does not provide efficacy or …
-
CLINICAL_TRIALS trial_result · 2026-03-09Clinical Trial Update: Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD) [Phase 3]
Phase 3 study of ataluren in nonsense mutation Duchenne muscular dystrophy has completed. The document provides a trial update but does not …
-
CLINICAL_TRIALS trial_result · 2026-03-09Clinical Trial Update: A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44 [Phase 1, Phase 2]
A Phase 1/2 study is evaluating the safety and efficacy of ENTR-601-44 in Duchenne muscular dystrophy. The trial is currently recruiting.
-
CLINICAL_TRIALS research · 2026-03-09Clinical Trial Update: A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety and Efficacy of ENTR-601-45 [Phase 1, Phase 2]
A Phase 1/2 clinical trial is evaluating the safety and potential efficacy of ENTR-601-45 for Duchenne muscular dystrophy that is amenable t…
-
CLINICAL_TRIALS research · 2026-03-06Clinical Trial Update: NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD) [Phase 2]
NS Pharma's NS-089/NCNP-02-201 is a Phase 2 trial for Duchenne muscular dystrophy in boys with exon 44 mutations, and recruitment is ongoing…
-
CLINICAL_TRIALS trial_result · 2026-03-06Clinical Trial Update: Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy [Phase 2]
This clinical trial update describes an open-label extension study of Wave Life Sciences' WVE-N531 for Duchenne Muscular Dystrophy in Phase …
-
CLINICAL_TRIALS research · 2026-03-04Clinical Trial Update: Trial of Cell Based Therapy for DMD [Phase 1]
Phase 1 clinical trial update for a cell-based therapy in Duchenne muscular dystrophy, currently recruiting.
-
CLINICAL_TRIALS research · 2026-03-03Clinical Trial Update: A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE) [Phase 3]
Phase 3 clinical trial update for SGT-003 gene therapy in ambulant males with Duchenne Muscular Dystrophy; the study is currently recruiting…
-
CLINICAL_TRIALS research · 2026-03-03Clinical Trial Update: Microdystrophin Gene Transfer Study in Adolescents and Children With DMD [Phase 1, Phase 2]
Solid Biosciences is running a Phase 1/2 microdystrophin gene transfer study in children and adolescents with Duchenne muscular dystrophy; t…
-
CLINICAL_TRIALS research · 2026-03-03Clinical Trial Update: A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE) [Phase 1, Phase 2]
Solid Biosciences is conducting the INSPIRE DUCHENNE study of SGT-003 gene therapy for Duchenne muscular dystrophy. The Phase 1/2 trial is c…
-
CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Relation Between Muscle Architecture and Functional Ability in Children With Duchenne Muscular Dystrophy
A completed clinical study investigating how muscle architecture relates to functional ability in children with Duchenne muscular dystrophy.
-
CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Effects of Posture and Quality of Life in Duchenne Muscular Dystrophy Children [NA]
A recruiting clinical trial sponsored by Riphah International University aims to examine how posture influences quality of life in children …
-
CLINICAL_TRIALS research · 2026-02-27Clinical Trial Update: Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb Muscles
An ongoing clinical trial at Sanko University is studying Duchenne muscular dystrophy and the viscoelastic properties of upper limb muscles,…
-
CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) [Phase 3]
Phase 3 study evaluating high-dose eteplirsen for Duchenne muscular dystrophy is currently active but not recruiting.
-
CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
Registry study update assessing long-term safety of vamorolone (AGAMREE) in Duchenne muscular dystrophy; the study is currently recruiting.
-
CLINICAL_TRIALS research · 2026-02-25Clinical Trial Update: Evaluation of the Role of miR-1 in the Pathogenesis and as a Biomarker in Muscular Dystrophies and Congenital Myopathies [NA]
A clinical trial is recruiting to evaluate the role of microRNA-1 (miR-1) in disease pathogenesis and as a biomarker for muscular dystrophie…