Duchenne Muscular Dystrophy
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CLINICAL_TRIALS trial_result · 2026-08-17Clinical Trial Update: A Phase 3 Study of TAS-205 in Patients With Duchenne Muscular Dystrophy（REACH-DMD） [Phase 3]
Phase 3 trial update for TAS-205 in Duchenne muscular dystrophy has completed for REACH-DMD study.
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CLINICAL_TRIALS trial_result · 2026-06-05Clinical Trial Update: A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy [Phase 3]
Phase 3 study of Deramiocel (CAP-1002) in ambulatory and non-ambulatory Duchenne muscular dystrophy patients is active but not recruiting.
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Can External Vagus Nerve Stimulation Reduce Systemic Levels of Inflammatory Mediators in Duchenne Muscular Dystrophy Patients? [NA]
A clinical trial is evaluating external vagus nerve stimulation to reduce systemic inflammatory mediators in Duchenne muscular dystrophy; en…
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CLINICAL_TRIALS trial_result · 2026-04-23Clinical Trial Update: A Study on Safety and Effectiveness of Long-term Treatment With Vamorolone in Boys With Duchenne Muscular Dystrophy [Phase 4]
Phase 4 study evaluating long-term safety and effectiveness of vamorolone in boys with Duchenne Muscular Dystrophy; current status is active…
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CLINICAL_TRIALS trial_result · 2026-04-23Clinical Trial Update: Feasibility of Virtual Reality in Children With Neuromuscular Disease, Effectiveness of Virtual Reality and Biofeedback [NA]
A completed clinical trial assessed the feasibility of virtual reality in children with neuromuscular diseases and evaluated the effectivene…
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CLINICAL_TRIALS trial_result · 2026-04-21Clinical Trial Update: Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting [Phase 4]
Phase 4 clinical trial update evaluating the safety and effectiveness of Sarepta's gene therapy Elevidys for Duchenne Muscular Dystrophy in …
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CLINICAL_TRIALS trial_result · 2026-04-20Clinical Trial Update: DMD- Interactive Virtual Reality Study [NA]
A completed clinical trial evaluating an interactive virtual reality study for Duchenne Muscular Dystrophy.
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CLINICAL_TRIALS trial_result · 2026-04-16Clinical Trial Update: Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders [NA]
A terminated clinical trial update investigating gut peptides and bone remodeling in children with neuromuscular disorders, sponsored by the…
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CLINICAL_TRIALS trial_result · 2026-04-09Clinical Trial Update: A Study to Assess the Efficacy and Safety of Satralizumab in Duchenne Muscular Dystrophy (DMD) [Phase 2]
This Phase 2 clinical trial update indicates that satralizumab is being studied for efficacy and safety in Duchenne muscular dystrophy, with…
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CLINICAL_TRIALS trial_result · 2026-04-08Clinical Trial Update: Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping
This clinical trial update describes the ongoing managed access program for Del-zota in participants with Duchenne muscular dystrophy mutati…
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CLINICAL_TRIALS trial_result · 2026-04-03Clinical Trial Update: An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy [Phase 4]
Phase 4 open-label study of golodirsen in non-ambulant Duchenne muscular dystrophy patients has been terminated.
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CLINICAL_TRIALS trial_result · 2026-03-24Clinical Trial Update: Long Term Follow-up for RGX-202
A clinical trial update on long-term follow-up for RGX-202 in Duchenne Muscular Dystrophy, with enrollment by invitation.
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CLINICAL_TRIALS trial_result · 2026-03-13Clinical Trial Update: Twice Weekly Steroids and Exercise as Therapy for DMD [Phase 2]
A Phase 2 clinical trial evaluating twice-weekly steroids and exercise as therapy for Duchenne Muscular Dystrophy has completed, with result…
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CLINICAL_TRIALS trial_result · 2026-03-10Clinical Trial Update: Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy [Phase 3]
Phase 3 trial update presenting long-term outcomes for ataluren in Duchenne muscular dystrophy; results were posted in March 2026.
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CLINICAL_TRIALS trial_result · 2026-03-09Clinical Trial Update: Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD) [Phase 3]
Phase 3 study of ataluren in nonsense mutation Duchenne muscular dystrophy has completed. The document provides a trial update but does not …
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CLINICAL_TRIALS trial_result · 2026-03-09Clinical Trial Update: A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety and Efficacy of ENTR-601-44 [Phase 1, Phase 2]
A Phase 1/2 study is evaluating the safety and efficacy of ENTR-601-44 in Duchenne muscular dystrophy. The trial is currently recruiting.
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CLINICAL_TRIALS trial_result · 2026-03-06Clinical Trial Update: Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy [Phase 2]
This clinical trial update describes an open-label extension study of Wave Life Sciences' WVE-N531 for Duchenne Muscular Dystrophy in Phase …
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CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) [Phase 3]
Phase 3 study evaluating high-dose eteplirsen for Duchenne muscular dystrophy is currently active but not recruiting.
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CLINICAL_TRIALS trial_result · 2026-02-27Clinical Trial Update: Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
Registry study update assessing long-term safety of vamorolone (AGAMREE) in Duchenne muscular dystrophy; the study is currently recruiting.
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CLINICAL_TRIALS trial_result · 2026-02-24Clinical Trial Update: Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
Registry update shows that the Translarna (ataluren) study in nonsense mutation Duchenne muscular dystrophy has completed.
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CLINICAL_TRIALS trial_result · 2026-02-17Clinical Trial Update: An Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its Long-Lasting Effects in DMD Patients (MUSCLE) [EARLY_Phase 1]
An open-label, multi-dose Phase 1 study evaluated the safety and potential long-lasting effects of a CRISPR gene-editing therapy in Duchenne…
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CLINICAL_TRIALS trial_result · 2026-02-13Clinical Trial Update: A Trial to Investigate Safety and Pharmacokinetics of GRT6019, Including Food Effect, in Healthy Male Participants [Phase 1]
Grünenthal GmbH completed a Phase 1 study to evaluate the safety, tolerability, and pharmacokinetics of GRT6019 in healthy male participants…
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CLINICAL_TRIALS trial_result · 2026-02-06Clinical Trial Update: A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study [Phase 3]
This update presents long-term follow-up data from participants who previously received delandistrogene moxeparvovec (SRP-9001) in a Duchenn…
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CLINICAL_TRIALS trial_result · 2026-01-26Clinical Trial Update: Oral Ifetroban in Subjects With Duchenne Muscular Dystrophy [Phase 2]
Phase 2 clinical trial update for oral ifetroban in Duchenne muscular dystrophy patients, including those with cardiomyopathy, completed wit…
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CLINICAL_TRIALS trial_result · 2026-01-14Clinical Trial Update: Virtual Reality and Whole Body Vibration on Muscle Strength and Balance in Children With DMD [NA]
A completed clinical trial from Cairo University evaluating the effects of virtual reality and whole body vibration on muscle strength and b…