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CLINICAL_TRIALS research · 2026-03-13

Clinical Trial Update: PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD) [Phase 1, Phase 2]

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Summary

Clinical trial update on PBGENE-DMD for Duchenne muscular dystrophy, outlining a Phase 1/2a safety and preliminary efficacy study that is not yet recruiting.

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Diseases / indications

Drugs mentioned

  • PBGENE-DMD

Snippet

Sponsor: Precision BioSciences, Inc. | Conditions: Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD | Phase 1, Phase 2 | Status: NOT_YET_RECRUITING