Catalyst Wire Dossier Catalyst Wire Dossier
CLINICAL_TRIALS trial_result · 2026-02-27

Clinical Trial Update: A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dystrophy (DMD) (MIS51ON) [Phase 3]

View source ↗

Summary

Phase 3 study evaluating high-dose eteplirsen for Duchenne muscular dystrophy is currently active but not recruiting.

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

Drugs mentioned

  • EXONDYS 51 (eteplirsen)

Snippet

Sponsor: Sarepta Therapeutics, Inc. | Conditions: Muscular Dystrophy, Duchenne | Phase 3 | Status: ACTIVE_NOT_RECRUITING