Duchenne Muscular Dystrophy
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2018-06-14Clinical Trial Update: A Study of the Safety, Tolerability & Efficacy of Long-term Administration of Drisapersen in US & Canadian Subjects [Phase 3]
This update notes the termination of a Phase 3 study evaluating long-term safety, tolerability, and efficacy of drisapersen in US and Canadi…
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CLINICAL_TRIALS trial_result · 2018-06-12Clinical Trial Update: Pulmonary and Upper Limb Functions in Duchenne Muscular Dystrophy
Trial update for a Duchenne Muscular Dystrophy study evaluating pulmonary and upper limb function, conducted by Hacettepe University; the tr…
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CLINICAL_TRIALS trial_result · 2018-05-30Clinical Trial Update: The Effect of Kinesiology Taping on Balance in Duchenne Muscular Dystrophy [NA]
A completed clinical trial evaluating whether kinesiology taping improves balance in individuals with Duchenne Muscular Dystrophy, sponsored…
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CLINICAL_TRIALS trial_result · 2018-05-24Clinical Trial Update: Lower Limb Flexibility in Duchenne Muscular Dystrophy: Effects on Functional Performance
This clinical trial update examines how lower limb flexibility affects functional performance in Duchenne muscular dystrophy, and the study …
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CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Historically Controlled Trial of Corticosteroids in Young Boys With Duchenne Muscular Dystrophy [Phase 2]
A Phase 2 historically controlled trial evaluating corticosteroids in young boys with Duchenne Muscular Dystrophy has completed with results…
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CLINICAL_TRIALS trial_result · 2018-05-18Clinical Trial Update: Kinesiology Taping in Duchenne Muscular Dystrophy: Effects on Performance, Gait Characteristics, and Energy Consumption [NA]
A completed clinical trial evaluated kinesiology taping for its impact on performance, gait characteristics, and energy consumption in Duche…
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CLINICAL_TRIALS research · 2018-05-15Clinical Trial Update: Evaluation of Muscle miRNA as Biomarkers in Dystrophinopathies [NA]
An update on a clinical trial evaluating muscle microRNAs as biomarkers in dystrophinopathies, including Duchenne and Becker muscular dystro…
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CLINICAL_TRIALS withdrawal · 2018-05-14Clinical Trial Update: Relationship Between PFTs and Pdi in DMD [NA]
A clinical trial evaluating the relationship between pulmonary function tests and transdiaphragmatic pressure in Duchenne muscular dystrophy…
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CLINICAL_TRIALS research · 2018-05-11Clinical Trial Update: Investigation Of Factors Affecting Hand Functions in Nonambulatory Patients With Duchenne Muscular Dystrophy
A completed clinical trial investigating factors affecting hand functions in nonambulatory Duchenne muscular dystrophy patients.
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CLINICAL_TRIALS research · 2018-04-27Clinical Trial Update: Effects of Fear of Falling on Physical Performance and Quality of Life in Children With Duchenne Muscular Dystrophy
Clinical trial update examining how fear of falling affects physical performance and quality of life in children with Duchenne Muscular Dyst…
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CLINICAL_TRIALS trial_result · 2018-04-19Clinical Trial Update: L-citrulline and Metformin in Duchenne's Muscular Dystrophy [Phase 3]
A Phase 3 clinical trial evaluating the combination of L-citrulline and metformin for Duchenne muscular dystrophy has completed. The study w…
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CLINICAL_TRIALS trial_result · 2018-04-05Clinical Trial Update: Where Does Hope Fit In? The Relationship Between Hope, Uncertainty, and Coping Efficacy in Mothers of Children With Duchenne/Becker Muscular Dystrophy
NHGRI-funded clinical trial update examining the relationship between hope, uncertainty, and coping efficacy among mothers of children with …
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CLINICAL_TRIALS research · 2018-04-05Clinical Trial Update: The PTC124 (Ataluren) Clinical Trial for Duchenne Muscular Dystrophy: Exploration of the Experiences of Parents, Clinician Researchers, and the Industry Sponsor
A completed clinical trial study examining the experiences of parents, clinician researchers, and the industry sponsor in the Ataluren (PTC1…
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CLINICAL_TRIALS trial_result · 2018-03-21Clinical Trial Update: Revatio for Heart Disease in Duchenne Muscular Dystrophy and Becker Muscular Dystrophy [Phase 2]
Phase 2 trial of Revatio (sildenafil) for Duchenne and Becker muscular dystrophy was terminated; results were posted in 2018.
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CLINICAL_TRIALS research · 2018-03-16Clinical Trial Update: Biomechanical and Morphological Changes in Dystrophic Muscle [NA]
This clinical trial update discusses biomechanical and morphological changes in dystrophic muscle related to Duchenne muscular dystrophy. Th…
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CLINICAL_TRIALS approval · 2018-02-28Clinical Trial Update: Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy
PTC Therapeutics' deflazacort (Emflaza) Expanded Access Program for Duchenne Muscular Dystrophy has been approved for marketing.
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FDA approval · 2018-02-08FDA Approved: EXONDYS 51 — Supplemental Application (Sarepta Therapeutics, Inc.)
The FDA approved a supplemental application for Exondys 51 (eteplirsen) submitted by Sarepta Therapeutics, Inc.
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CLINICAL_TRIALS trial_result · 2018-02-01Clinical Trial Update: Effect of EPA and DHA in the Inflammation and Metabolic Disorders in DMD/DMB Patients [NA]
A completed clinical trial evaluated the effects of eicosapentaenoic acid (EPA) and docosahexaenoic acid (DHA) on inflammation and metabolic…
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CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort [Phase 1]
An open-label, long-term extension study assessed the safety and tolerability of deflazacort in Duchenne Muscular Dystrophy; the trial has c…
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CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: A Prospective Natural History Study of Progression of Subjects With Duchenne Muscular Dystrophy.
A prospective natural history study of Duchenne Muscular Dystrophy sponsored by BioMarin has been terminated.
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CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy [Phase 1, Phase 2]
A Phase 1/2 study of PRO045 in Duchenne muscular dystrophy has been terminated. The termination status is indicated in the trial update.
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CLINICAL_TRIALS withdrawal · 2017-12-08Clinical Trial Update: A Phase I/II Study of BMN053 in Subjects With Duchenne Muscular Dystrophy (DMD) [Phase 1, Phase 2]
Phase I/II study of BMN053 for Duchenne muscular dystrophy has been terminated.
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CLINICAL_TRIALS trial_result · 2017-12-08Clinical Trial Update: Open Label, Extension Study of PRO044 in Duchenne Muscular Dystrophy (DMD) [Phase 2]
Open-label extension study of PRO044 in Duchenne muscular dystrophy (Phase 2) has been terminated.
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CLINICAL_TRIALS trial_result · 2017-11-24Clinical Trial Update: Clinical Intramuscular Gene Transfer Trial of rAAVrh74.MCK.Micro-Dystrophin to Patients With Duchenne Muscular Dystrophy [Phase 1]
Phase 1 intramuscular gene transfer trial using rAAVrh74.MCK.Micro-Dystrophin for Duchenne Muscular Dystrophy has completed.
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CLINICAL_TRIALS trial_result · 2017-10-16Clinical Trial Update: A Clinical Study to Assess Two Doses of GSK2402968 in Subjects With Duchenne Muscular Dystrophy (DMD) [Phase 2]
A Phase 2 study evaluating two doses of GSK2402968 in Duchenne muscular dystrophy has completed, with results posted in October 2017.