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CLINICAL_TRIALS approval · 2018-02-28

Clinical Trial Update: Deflazacort Expanded Access Program for Children, Adolescents and Adults With Duchenne Muscular Dystrophy

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Summary

PTC Therapeutics' deflazacort (Emflaza) Expanded Access Program for Duchenne Muscular Dystrophy has been approved for marketing.

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Diseases / indications

Drugs mentioned

  • EMFLAZA (deflazacort)

Snippet

Sponsor: PTC Therapeutics | Conditions: Duchenne Muscular Dystrophy | Status: APPROVED_FOR_MARKETING